One of the most devastating diseases finally has a treatment that can slow its progression and transform lives, tearful ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

Pivotal results from uniQure’s gene therapy for Huntington’s disease have brought new light to patients who have known only ...

A new medical trial showed promising results as scientists seek a breakthrough to treat Huntington's disease, according to research team based in the United Kingdom. The clinical drug trial by ...

However, in late September 2025, scientists successfully treated Huntington’s for the first time in a ground-breaking study.

Families are elated by news of the first treatment for Huntington's disease - but when and how will the NHS fund it?

Huntington’s disease (HD) is a condition that is hereditary and causes nerve cells in specific parts of the brain to slowly deteriorate and die. The disorder affects regions responsible for controlled ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

An experimental gene therapy seems to show potential to slow the debilitating progression of Huntington's disease, a European ...

An experimental gene therapy slowed Huntington’s by up to 75 percent in a small clinical trial. While not a cure, it may give patients longer lives.

Maureen Graham with her grandson, Alex, who was diagnosed with Huntington’s disease when he was 30 - Gareth Iwan Jones It was only this morning, as Maureen Graham was leaving Mass, when the ...

Huntington’s disease is a rare, inherited neurodegenerative disorder that eventually damages brain cells, resulting in movement challenges, cognitive decline, and psychiatric issues. Symptoms usually ...